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Aug 27, 2026 · Archive
Science

FDA Approves LISRAYA, First Oral Drug For Adult Dermatomyositis

Priovant's once-daily pill beat placebo in the largest dermatomyositis trial ever run, cutting patients' reliance on chronic steroids.

  • Brepocitinib scored 46.5 on the Total Improvement Score at week 52, versus 31.2 for placebo.
  • 55% of drug patients hit moderate improvement with minimal or no steroids, versus 30% on placebo.
  • Among heavier steroid users, 45% quit corticosteroids entirely, compared with 29% given placebo.

Why it matters: Until now, the only remedy was a steroid dose harsh enough to become its own disease.

FDA Press ↗ · Aug 27, 20268/27/26